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Fact Sheet
Currently, there are different gene therapy approaches available through clinical trials.
… before birth (during fetal development). After birth, a gene that codes for a blocking protein (BCL11A) is turned on. … complications. … To understand sickle cell disease and gene therapy , you should first know about blood cells and the …
For Teachers
A microbiome is all of the genetic material found in a microbe, such as a bacterium, fungal cell or virus.
… found in a microbe, such as a bacterium, fungal cell or virus. It also may refer to the genetic material found in a … found in a microbe, such as a bacterium, fungal cell or virus. ​ … Microbiome, Microbes, Genetic Material, Microbial DNA, Gut DNA, Fungus, Bacteria, Virus, Microbial Genome … A microbiome is all of the genetic …
News Release
Doctors and researchers reunite with patient who received gene therapy for GM1 gangliosidosis.
… Doctors and researchers reunite with patient who received gene therapy for GM1 gangliosidosis. … In a sun-lit conference … after Jojo attended the last tea party, she received gene therapy for her rare disorder, GM1 gangliosidosis. … …
Educational Resources
A gene pool is the total genetic diversity found within a population or a species.
… Gene Pool … A gene pool is the total genetic diversity found within a … Diversity, Genes, Extinction, Population Genetics … A gene pool refers to the combination of all the genes … present in a reproducing population or species. A large gene pool has extensive genomic diversity and is better able …
News Release
A team from the NIH has surmounted a major obstacle to testing potential drug therapies for a rare, genetic condition called Gaucher disease.
… is an inherited condition caused by alterations in the GBA gene. It affects one in every 50,000 to 100,000 people, but … called Gaucher disease. ​ … Gaucher disease, drug therapy for Gaucher disease, Ellen Sidransky Ph.D., GBA gene alterations, glucocerebroside accumulation … A team from …
Educational Resources
An antibody is a protein component of the immune system that circulates in the blood, recognizes foreign substances like bacteria and viruses, and neutralizes them.
… viruses, and neutralizes them. … Immune System, Bacteria, Virus, Blood, Circulation, Disease, Antigen … An antibody is …
Educational Resources
The microbiome is a term used to describe the specific collection of microorganisms (such as fungi, bacteria and viruses) that exist in a particular environment.
… Microbiome Project, Microbe, Microorganism, Bacteria, Virus, Genetic Material … The microbiome is the community of …
Clinical Research
GENE-FORECAST® is developing a community cohort and resource for defining the significance of ancestry-related genomic variation in African-Americans.
… of Cardiovascular Disease in Africans Americans Study (GENE-FORECAST®) study is developing a community-based cohort … ancestry-related genomic variation in African-Americans. … GENE-FORECAST® will test the working hypothesis that … efforts will yield novel ancestry-related DNA variants associated with the CVD. Accordingly, our protocol also …
Educational Resources
Gene mapping is the process of establishing the locations of genes on the chromosomes.
… Gene Mapping … Gene mapping is the process of establishing the locations of … Analysis, Genome Sequencing, DNA Sequencing, Chromosomes … Gene mapping refers to the process of determining the … on chromosomes. Today, the most efficient approach for gene mapping involves sequencing a genome and then using …
Educational Resources
Gene amplification is an increase in the number of copies of a gene sequence.
… Gene Amplification … Gene amplification is an increase in the number of copies of a gene sequence. … DNA Sequence, Cancer, PCR, Polymerase Chain …